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Figure 5 | Genetic Vaccines and Therapy

Figure 5

From: Lentiviral-mediated gene correction of mucopolysaccharidosis type IIIA

Figure 5

Urine analysis. Urine from selected mice was analysed by gradient PAGE as described in Materials and methods. Lane M, octasaccharide size standard; lane 1, empty; lane 2, normal; lane 3, normal; lane 4, MPS IIIA; lane 5, MPS IIIA; lane 6, treated #2, 54 days post-treatment; lane 7, treated #2, 122 days post-treatment; lane 8, treated #3, 67 days post-treatment; lane 9, treated #7, 61 days post-treatment; lane 10, treated #7, 196 days post-treatment; lane 11, treated #94, 106 days post-treatment; lane 12, treated #98, 98 days post-treatment.

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